Past Exhibiting Companies

2023 Exhibitors & Patient Advocate Showcase

Amicus Therapeutics
Sanofi
Takeda Pharmaceutical Company Limited
Chiesi Global Rare Diseases
JCR Pharmaceuticals Co., Ltd.
4D Molecular Therapeutics (4DMT)
Astellas Gene Therapies
BioMarin Pharmaceutical
Orchard Therapeutics
Passage Bio
Ultragenyx
Aeglea BioTherapeutics
ARCHIMEDlife
Azafaros
Denali Therapeutics
Freeline Therapeutics
Greenwood Genetic Center
Homology Medicines, Inc.
Horizon Therapeutics
Immusoft Corporation
Inozyme
KemPharm Inc
Lysosomal & Rare Disorders Research & Treatment Center, Inc
Protalix Ltd
QPS LLC
Recordati Rare Diseases
REGENXBIO Inc.
Travere Therapeutics
Worldwide Clinical Trials

Associação Sanfilippo Portugal
Cure GM1 Foundation
Cure Sanfilippo Foundation
Gaucher Community Alliance
International Gaucher Alliance
Living in the Light of Rare Diseases
MLD Foundation
National MPS Society
National Organization for Rare Disorders
National Tay-Sachs & Allied Diseases Assoc. (NTSAD)
Pompe Support Network

2022 Exhibitors & Patient Advocate Showcase

Amicus Therapeutics
4DMT
Aceragen
Aeglea BioTherapeutics
AllStripes Research Inc.
Amicus Therapeutics
ARCHIMEDlife
Astellas Gene Therapies
AVROBIO
Azafaros
BioMarin Pharmaceutical Inc.
Chiesi Global Rare Diseases
Denali Therapeutics
European GD Network Charitable Foundation
Freeline Therapeutics Ltd
Greenwood Genetic Center
Homology Medicines, Inc.
Idorsia Pharmaceuticals Ltd
Igenomix
JCR Pharmaceuticals Co., Ltd.
Lysosomal & Rare Disorder Research & Treatment Center
M6P Therapeutics (M6PT)
Neurogene Inc.
Orchard Therapeutics
Orphazyme A/S
Paradigm Biopharmaceuticals
Passage Bio
Pfizer
Rare Disease Data Trust (RDDT)
REGENXBIO Inc.
Sanofi Genzyme
SEI Healthcare
Sigilon Therapeutics
Spark Therapeutics
Takeda Pharmaceuticals
Taysha Gene Therapies
Travere Therapeutics
Ultragenyx Pharmaceutical Inc.

Batten Disease Support and Research Association
Cure GM1 Foundation
Cure Sanfilippo Foundation
Global Genes
The International Working Group on Gaucher Disease (IWGGD)
Living in the Light
MLD Foundation
National MPS Society
NORD
NTSAD (National Tay-Sachs & Allied Diseases Association)

2021 Exhibitors & Patient Advocate Showcase

Amicus Therapeutics
AskBio
Audentes Therapeutics, an Astellas Company
BioMarin Pharmaceutical
CENTOGENE GmbH
Chiesi Global Rare Diseases
Denali Therapeutics, Inc.
Freeline
Forge Biologics
Homology Medicines, Inc.
Idorsia Pharmaceutical
Invitae
JCR Pharmaceuticals Co., Ltd.
Orchard Therapeutics
Orphazyme
Passage Bio
Pfizer
QPS Austria GmbH
Sanofi Genzyme
Sigilon Therapeutics
Spark Therapeutics
Takeda
Travere Therapeutics
Ultragenyx Pharmaceutical Inc.

Batten Disease Support and Research Association
Cure GM1 Foundation
Cure Sanfilippo Foundation
Fabry International Network
National MPS Society
United MSD Foundation

2020 Exhibitors & Patient Advocate Showcase

Amicus Therapeutics, Inc.
ARCHIMEDlife
Audentes Therapeutics
Baebies
BioMarin Pharmaceutical
Blueprint Genetics
CENTOGENE US LLC
Charles River
Chiesi Farmaceutici S.p.A.
Denali Therapeutics
Enzyvant
European GD Network
Greenwood Genetic Center
Homology Medicines, Inc.
Idorsia Pharmaceutical
Invitae
JCR Pharmaceuticals Co., Ltd.
Lysosomal & Rare Disorders Research & Treatment Center (LDRTC)
Neurogene Inc.
Orchard Therapeutics
Orphazyme
Patient Discovery
Pfizer, Inc.
PROMETRIKA, LLC
Protalix Ltd.
QPS Austria GmbH
Rare Disease Research
Retrophin, Inc.
Sanofi Genzyme
Sigilon Therapeutics
Spark Therapeutics
Takeda Pharmaceuticals
Ultragenyx Pharmaceutical

Batten Disease Support and Research Association
Cure Sanfilippo Foundation
European Working Group on Gaucher Disease
EveryLife Foundation for Rare Diseases
Fabry International Network
Global Genes
MLD Foundation
MSD Action Foundation
National Fabry Disease Foundation
National MPS Society
Salla Treatment and Research Foundation
United MSD Foundation

2019 Exhibitors & Patient Advocate Showcase

Alexion Pharmaceuticals
Amicus Therapeutics, Inc.
Audentes Therapeutics
Bio Insight Group
BioMarin Pharmaceutical
Carbosynth LLC
Chiesi Farmaceutici S.p.A.
Diplomat Specialty Infusion Group
Enzyvant
European Gaucher Disease Network
Fairview Specialty Pharmacy
Greenwood Genetic Center
Invitae
JCR Pharmaceuticals Co., Ltd.
Lukare Medical, LLC
Lysogene
Lysosomal & Rare Disorders Research
& Treatment Center (LDRTC)
Mayo Medical Laboratories
Pfizer, Inc.
Protalix Ltd.
QPS Austria GmbH
Retrophin, Inc.
Sangamo Therapeutics, Inc.
Sanofi Genzyme
Swedish Orphan Biovitrum AB
Takeda
Ultragenyx Pharmaceutical

Batten Disease Support and Research Association
Cure GMI 1 Foundation
Cure Sanfilippo Foundation
Every Life Foundation for Rare Diseases
Global Genes
Living in the Light
MLD Foundation
National Fabry Disease Foundation
National MPS Society
NORD
STAR Foundation

2018 Exhibitors & Patient Advocate Showcase

Alexion Pharmaceuticals, Inc.
Amicus Therapeutics, Inc.
Audentes Therapeutics
Baebies
BioMarin Pharmaceutical
Carbosynth
Chiesi Farmaceutici S.p.A.
Fairview Specialty Pharmacy
GlycoAnalytics, UC San Diego
Greenwood Genetic Center
Invitae
Lysosomal & Rare Disorders Research & Treatment Center (LDRTC)
Mayo Medical Laboratories
Pfizer, Inc.
Protalix Ltd.
QPS Austria GmbH
Rare Disease Report
Sangamo Therapeutics
Sanofi Genzyme
Shire
Ultragenyx Pharmaceutical

Cure Sanfilippo Foundation
EveryLife Foundation for Rare Diseases
Global Genes
Jonah’s Just Begun
MLD Foundation
National MPS Society
National Organization of Rare Disorders (NORD)
Project Alive

2017 Exhibitors & Patient Advocate Showcase

Alexion Pharmaceuticals, Inc.
Amicus Therapeutics, Inc.
BioMarin Pharmaceutical
Carbosynth LLC
Fairview Specialty Pharmacy
GSK
Greenwood Genetic Center
Horizon Pharma
Invitae
Lysosomal & Rare Disorders Research & Treatment Center (LDRTC)
Mayo Medical Laboratories
Pfizer, Inc.
Protalix Ltd.
Rare Disease Report
Sangamo BioSciences, Inc.
Sanofi Genzyme
Shire
ThinkGenetic Foundation
Ultragenyx Pharmaceutical

Batten Disease Support and Research Association
Cure Sanfilippo Foundation
EveryLife Foundation for Rare Diseases
Global Genes
Jonah’s Just Begun
LAL SOLACE
MLD Foundation
National MPS Society
National Organization of Rare Disorders (NORD)

2016 Exhibitors & Patient Advocate Showcase

Alexion Pharmaceuticals, Inc.
American College of Medical Genetics and Genomics
Amicus Therapeutics
BioMarin Pharmaceutical Inc.
Carbosynth LLC
Emory Genetics Laboratory
Fairview Specialty Pharmacy
The Greenwood Genetic Center
Living in the Light
Lysosomal & Rare Disorders Research Center
Mayo Medical Laboratories
Orsini Healthcare
Pfizer Inc.
Protalix Biotherapeutics
Raptor Pharmaceutical Corp.
Rare Disease Report
Retrophin
Sangamo BioSciences, Inc.
Sanofi Genzyme
Shire International
Shire
Ultragenyx Pharmaceutical Inc.

Batten Disease Support and Research Association
Fight NPC
Global Genes
Jonah’s Just Begun
LAL Solace
National Fabry Disease Foundation
National Organization of Rare Disorders

2015 Exhibitors

Amicus Therapeutics
Alexion Pharmaceuticals, Inc.
Batten Disease Support and Research Association
BioMarin Pharmaceutical Inc.
The Fabry Support and Information Group
Genzyme, a Sanofi company
The Greenwood Genetic Center
InsideMD
The International Society for Mannosidosis and Related Diseases (ISMRD)
LAL Aware
Lukare Medical, LLC
Lysosomal & Rare Disorders Research & Treatment CenterMLD Foundation
Newborn Screening Translational Research Network (NBSTRN)
Orsini Healthcare
Pfizer Inc.
Raptor Pharmaceutical Corp.
Rare Disease Report
Shire International
Shire Pharmaceuticals
Synageva BioPharma
Ultragenyx Pharmaceutical Inc.
University of Minnesota and Fairview Pharmacy Services

Content last updated on May 3rd, 2023 at 12:28 pm